To some of you, those numbers and letters mean absolutely nothing. For a few of you, those random numbers and letters may change your entire future.
VX-770 is a medication for people with cystic fibrosis that has produced incredible results in Phase 3 clinical trials. It is the first medication of it's kind, targeting the actual gene defect rather than simply treating the symptoms. Revolutionary, life-changing and miraculous are all words I've heard people using to describe this drug.
Only about 4% of the CF population has the specific gene the VX-770 targets (G551D). I am not part of that 4%, but this is still HUGE news. It is an enormous leap forward; a stepping stone to a drug that will someday help everyone with CF, and it is one step closer to a cure. I'm not one to get all giddy when I hear about most drug trials, and hearing "a cure will be found in the next few years" gets old after hearing it for 15+ years. But you guys, there is proof backing this up. IT'S WORKING, and that is something to be excited about!
A couple articles about VX-770: